New therapeutic strategies for hemoglobinopathies an other hereditary anemias. From the bench to the bed side.

A.Y. 2019/2020
Lesson for
2
ECTS
11
Overall hours
Lesson period
July
Language
English
The aim of the course is to deepen the knowledge of how new therapeutic strategies develop from the understanding of pathophysiology and molecular basis of genetic pathologies (i.e. thalassemia syndromes, sickle cell disease and other hereditary anemias). In particular, the development of gene therapy, of new pharmacological molecules that target pathways involved in the development of the disease and the role of modifier genes as potential therapeutic targets will be addressed.
Undefined
Assessment methods
Giudizio di approvazione
Assessment result
superato/non superato