New therapeutic strategies for hemoglobinopathies an other hereditary anemias. from the bench to the bed side.

A.A. 2019/2020
Insegnamento per
2
Crediti
11
Ore totali
Periodo
Luglio
Lingua
Inglese
The aim of the course is to deepen the knowledge of how new therapeutic strategies develop from the understanding of pathophysiology and molecular basis of genetic pathologies (i.e. thalassemia syndromes, sickle cell disease and other hereditary anemias). In particular, the development of gene therapy, of new pharmacological molecules that target pathways involved in the development of the disease and the role of modifier genes as potential therapeutic targets will be addressed.
Non definiti
Modalità di valutazione
Giudizio di approvazione
Giudizio di valutazione
superato/non superato